Actively Recruiting

Phase 3
Age: 4Years - 21Years
All Genders
NCT05382338

A Study of Treatment for Medulloblastoma Using Sodium Thiosulfate to Reduce Hearing Loss

Led by Children's Oncology Group · Updated on 2026-05-05

225

Participants Needed

105

Research Sites

358 weeks

Total Duration

On this page

Sponsors

C

Children's Oncology Group

Lead Sponsor

N

National Cancer Institute (NCI)

Collaborating Sponsor

AI-Summary

What this Trial Is About

This phase III trial tests two hypotheses in patients with low-risk and average-risk medulloblastoma. Medulloblastoma is a type of cancer that occurs in the back of the brain. The term, risk, refers to the chance of the cancer coming back after treatment. Subjects with low-risk medulloblastoma typically have a lower chance of the cancer coming back than subjects with average-risk medulloblastoma. Although treatment for newly diagnosed average-risk and low-risk medulloblastoma is generally effective at treating the cancer, there are still concerns about the side effects of such treatment. Side effects or unintended health conditions that arise due to treatment include learning difficulties, hearing loss or other issues in performing daily activities. Standard therapy for newly diagnosed average-risk or low-risk medulloblastoma includes surgery, radiation therapy, and chemotherapy (including cisplatin). Cisplatin may cause hearing loss as a side effect. In the average-risk medulloblastoma patients, this trial tests whether the addition of sodium thiosulfate (STS) to standard of care chemotherapy and radiation therapy reduces hearing loss. Previous studies with STS have shown that it may help reduce or prevent hearing loss caused by cisplatin. In the low-risk medulloblastoma patients, the study tests whether a less intense therapy (reduced radiation) can provide the same benefits as the more intense therapy. The less intense therapy may cause fewer side effects. Radiation therapy uses high energy x-rays to kill tumor cells and shrink tumors. Cisplatin is in a class of medications known as platinum-containing compounds. It works by killing, stopping or slowing the growth of cancer cells. The overall goals of this study are to see if giving STS along with standard treatment (radiation therapy and chemotherapy) will reduce hearing loss in medulloblastoma patients and to compare the overall outcome of patients with medulloblastoma treated with STS to patients treated without STS on a previous study in order to make sure that survival and recurrence of tumor is not worsened.

CONDITIONS

Official Title

A Study of Treatment for Medulloblastoma Using Sodium Thiosulfate to Reduce Hearing Loss

Who Can Participate

Age: 4Years - 21Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Patients aged 4 to 21 years at enrollment
  • Suspected newly diagnosed medulloblastoma by institutional diagnosis
  • Signed informed consent for eligibility screening and molecular characterization
  • Submission of required specimens within 5 days of surgery
  • Rapid central pathology, molecular, imaging, and audiology review confirming diagnosis and eligibility
  • No metastatic disease on brain or spine MRI
  • Residual tumor area less than or equal to 1.5 cm squared after surgery
  • Negative lumbar cerebrospinal fluid cytology obtained no sooner than 14 days after surgery
  • Weight over 10 kilograms
  • Enrollment and start of therapy within 31 days after diagnostic surgery
  • Adequate blood counts and kidney and liver function within 7 days prior to enrollment
  • Central nervous system function adequate; seizure disorder allowed if well controlled
  • Normal hearing in at least one ear confirmed by central audiology review
  • Compliance with all institutional, FDA, and NCI human study requirements
Not Eligible

You will not qualify if you...

  • Presence of metastatic disease by MRI or cerebrospinal fluid cytology
  • Inability to undergo lumbar puncture for cerebrospinal fluid assessment
  • Prior radiation or chemotherapy treatment except surgery or corticosteroids
  • Known allergy to sodium thiosulfate, sulfates/sulfites, or related thiol agents
  • Pregnancy or breastfeeding
  • Sexually active patients of reproductive potential not agreeing to use effective contraception during study participation

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 105 locations

1

Children's Hospital of Alabama

Birmingham, Alabama, United States, 35233

Active, Not Recruiting

2

USA Health Strada Patient Care Center

Mobile, Alabama, United States, 36604

Actively Recruiting

3

Phoenix Childrens Hospital

Phoenix, Arizona, United States, 85016

Actively Recruiting

4

Arkansas Children's Hospital

Little Rock, Arkansas, United States, 72202-3591

Actively Recruiting

5

Loma Linda University Medical Center

Loma Linda, California, United States, 92354

Actively Recruiting

6

Miller Children's and Women's Hospital Long Beach

Long Beach, California, United States, 90806

Actively Recruiting

7

Children's Hospital Los Angeles

Los Angeles, California, United States, 90027

Actively Recruiting

8

Valley Children's Hospital

Madera, California, United States, 93636

Actively Recruiting

9

Kaiser Permanente-Oakland

Oakland, California, United States, 94611

Actively Recruiting

10

Children's Hospital of Orange County

Orange, California, United States, 92868

Actively Recruiting

11

University of California Davis Comprehensive Cancer Center

Sacramento, California, United States, 95817

Actively Recruiting

12

Rady Children's Hospital - San Diego

San Diego, California, United States, 92123

Actively Recruiting

13

UCSF Medical Center-Mission Bay

San Francisco, California, United States, 94158

Actively Recruiting

14

Children's Hospital Colorado

Aurora, Colorado, United States, 80045

Actively Recruiting

15

Connecticut Children's Medical Center

Hartford, Connecticut, United States, 06106

Actively Recruiting

16

Yale University

New Haven, Connecticut, United States, 06520

Actively Recruiting

17

Alfred I duPont Hospital for Children

Wilmington, Delaware, United States, 19803

Actively Recruiting

18

Children's National Medical Center

Washington D.C., District of Columbia, United States, 20010

Actively Recruiting

19

Golisano Children's Hospital of Southwest Florida

Fort Myers, Florida, United States, 33908

Actively Recruiting

20

Memorial Regional Hospital/Joe DiMaggio Children's Hospital

Hollywood, Florida, United States, 33021

Actively Recruiting

21

Nemours Children's Clinic-Jacksonville

Jacksonville, Florida, United States, 32207

Actively Recruiting

22

University of Miami Miller School of Medicine-Sylvester Cancer Center

Miami, Florida, United States, 33136

Actively Recruiting

23

Nicklaus Children's Hospital

Miami, Florida, United States, 33155

Actively Recruiting

24

Arnold Palmer Hospital for Children

Orlando, Florida, United States, 32806

Actively Recruiting

25

Nemours Children's Hospital

Orlando, Florida, United States, 32827

Actively Recruiting

26

Nemours Children's Clinic - Pensacola

Pensacola, Florida, United States, 32504

Actively Recruiting

27

Saint Joseph's Hospital/Children's Hospital-Tampa

Tampa, Florida, United States, 33607

Actively Recruiting

28

Children's Healthcare of Atlanta - Arthur M Blank Hospital

Atlanta, Georgia, United States, 30329

Actively Recruiting

29

Kapiolani Medical Center for Women and Children

Honolulu, Hawaii, United States, 96826

Actively Recruiting

30

University of Illinois

Chicago, Illinois, United States, 60612

Actively Recruiting

31

Saint Jude Midwest Affiliate

Peoria, Illinois, United States, 61637

Actively Recruiting

32

Southern Illinois University School of Medicine

Springfield, Illinois, United States, 62702

Actively Recruiting

33

Riley Hospital for Children

Indianapolis, Indiana, United States, 46202

Actively Recruiting

34

Blank Children's Hospital

Des Moines, Iowa, United States, 50309

Actively Recruiting

35

University of Iowa/Holden Comprehensive Cancer Center

Iowa City, Iowa, United States, 52242

Actively Recruiting

36

Norton Children's Hospital

Louisville, Kentucky, United States, 40202

Actively Recruiting

37

Children's Hospital New Orleans

New Orleans, Louisiana, United States, 70118

Actively Recruiting

38

Sinai Hospital of Baltimore

Baltimore, Maryland, United States, 21215

Actively Recruiting

39

Johns Hopkins University/Sidney Kimmel Cancer Center

Baltimore, Maryland, United States, 21287

Actively Recruiting

40

Massachusetts General Hospital Cancer Center

Boston, Massachusetts, United States, 02114

Actively Recruiting

41

C S Mott Children's Hospital

Ann Arbor, Michigan, United States, 48109

Actively Recruiting

42

Children's Hospital of Michigan

Detroit, Michigan, United States, 48201

Actively Recruiting

43

Corewell Health Children's

Royal Oak, Michigan, United States, 48073

Actively Recruiting

44

Children's Hospitals and Clinics of Minnesota - Minneapolis

Minneapolis, Minnesota, United States, 55404

Actively Recruiting

45

Mayo Clinic in Rochester

Rochester, Minnesota, United States, 55905

Actively Recruiting

46

University of Mississippi Medical Center

Jackson, Mississippi, United States, 39216

Suspended

47

Children's Mercy Hospitals and Clinics

Kansas City, Missouri, United States, 64108

Actively Recruiting

48

Cardinal Glennon Children's Medical Center

St Louis, Missouri, United States, 63104

Actively Recruiting

49

Washington University School of Medicine

St Louis, Missouri, United States, 63110

Actively Recruiting

50

Children's Hospital and Medical Center of Omaha

Omaha, Nebraska, United States, 68114

Actively Recruiting

51

University of Nebraska Medical Center

Omaha, Nebraska, United States, 68198

Actively Recruiting

52

Saint Peter's University Hospital

New Brunswick, New Jersey, United States, 08901

Actively Recruiting

53

Rutgers Cancer Institute of New Jersey-Robert Wood Johnson University Hospital

New Brunswick, New Jersey, United States, 08903

Actively Recruiting

54

Newark Beth Israel Medical Center

Newark, New Jersey, United States, 07112

Actively Recruiting

55

Saint Joseph's Regional Medical Center

Paterson, New Jersey, United States, 07503

Actively Recruiting

56

Albany Medical Center

Albany, New York, United States, 12208

Actively Recruiting

57

Roswell Park Cancer Institute

Buffalo, New York, United States, 14263

Actively Recruiting

58

The Steven and Alexandra Cohen Children's Medical Center of New York

New Hyde Park, New York, United States, 11040

Actively Recruiting

59

Laura and Isaac Perlmutter Cancer Center at NYU Langone

New York, New York, United States, 10016

Actively Recruiting

60

Mount Sinai Hospital

New York, New York, United States, 10029

Actively Recruiting

61

Stony Brook University Medical Center

Stony Brook, New York, United States, 11794

Actively Recruiting

62

State University of New York Upstate Medical University

Syracuse, New York, United States, 13210

Actively Recruiting

63

Montefiore Medical Center - Moses Campus

The Bronx, New York, United States, 10467

Actively Recruiting

64

New York Medical College

Valhalla, New York, United States, 10595

Actively Recruiting

65

UNC Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, United States, 27599

Actively Recruiting

66

Carolinas Medical Center/Levine Cancer Institute

Charlotte, North Carolina, United States, 28203

Actively Recruiting

67

East Carolina University

Greenville, North Carolina, United States, 27834

Actively Recruiting

68

Wake Forest University Health Sciences

Winston-Salem, North Carolina, United States, 27157

Actively Recruiting

69

Sanford Broadway Medical Center

Fargo, North Dakota, United States, 58122

Actively Recruiting

70

Children's Hospital Medical Center of Akron

Akron, Ohio, United States, 44308

Actively Recruiting

71

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States, 45229

Actively Recruiting

72

Rainbow Babies and Childrens Hospital

Cleveland, Ohio, United States, 44106

Actively Recruiting

73

Nationwide Children's Hospital

Columbus, Ohio, United States, 43205

Actively Recruiting

74

Dayton Children's Hospital

Dayton, Ohio, United States, 45404

Actively Recruiting

75

ProMedica Toledo Hospital/Russell J Ebeid Children's Hospital

Toledo, Ohio, United States, 43606

Actively Recruiting

76

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States, 73104

Actively Recruiting

77

Legacy Emanuel Children's Hospital

Portland, Oregon, United States, 97227

Actively Recruiting

78

Oregon Health and Science University

Portland, Oregon, United States, 97239

Actively Recruiting

79

Geisinger Medical Center

Danville, Pennsylvania, United States, 17822

Actively Recruiting

80

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

81

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, United States, 15224

Actively Recruiting

82

Rhode Island Hospital

Providence, Rhode Island, United States, 02903

Actively Recruiting

83

Prisma Health Richland Hospital

Columbia, South Carolina, United States, 29203

Actively Recruiting

84

BI-LO Charities Children's Cancer Center

Greenville, South Carolina, United States, 29605

Actively Recruiting

85

Sanford USD Medical Center - Sioux Falls

Sioux Falls, South Dakota, United States, 57117-5134

Actively Recruiting

86

Vanderbilt University/Ingram Cancer Center

Nashville, Tennessee, United States, 37232

Suspended

87

Dell Children's Medical Center of Central Texas

Austin, Texas, United States, 78723

Actively Recruiting

88

Driscoll Children's Hospital

Corpus Christi, Texas, United States, 78411

Actively Recruiting

89

Medical City Dallas Hospital

Dallas, Texas, United States, 75230

Actively Recruiting

90

UT Southwestern/Simmons Cancer Center-Dallas

Dallas, Texas, United States, 75390

Actively Recruiting

91

El Paso Children's Hospital

El Paso, Texas, United States, 79905

Actively Recruiting

92

Children's Hospital of San Antonio

San Antonio, Texas, United States, 78207

Actively Recruiting

93

University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States, 78229

Actively Recruiting

94

University of Virginia Cancer Center

Charlottesville, Virginia, United States, 22908

Actively Recruiting

95

VCU Massey Comprehensive Cancer Center

Richmond, Virginia, United States, 23298

Actively Recruiting

96

Seattle Children's Hospital

Seattle, Washington, United States, 98105

Actively Recruiting

97

Providence Sacred Heart Medical Center and Children's Hospital

Spokane, Washington, United States, 99204

Actively Recruiting

98

Mary Bridge Children's Hospital and Health Center

Tacoma, Washington, United States, 98405

Actively Recruiting

99

University of Wisconsin Carbone Cancer Center - University Hospital

Madison, Wisconsin, United States, 53792

Actively Recruiting

100

Marshfield Medical Center-Marshfield

Marshfield, Wisconsin, United States, 54449

Actively Recruiting

101

Children's Hospital of Wisconsin

Milwaukee, Wisconsin, United States, 53226

Actively Recruiting

102

IWK Health Centre

Halifax, Nova Scotia, Canada, B3K 6R8

Actively Recruiting

103

Centre Hospitalier Universitaire Sainte-Justine

Montreal, Quebec, Canada, H3T 1C5

Actively Recruiting

104

Centre Hospitalier Universitaire de Sherbrooke-Fleurimont

Sherbrooke, Quebec, Canada, J1H 5N4

Actively Recruiting

105

CHU de Quebec-Centre Hospitalier de l'Universite Laval (CHUL)

Québec, Canada, G1V 4G2

Actively Recruiting

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How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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