Actively Recruiting

Phase 1
Age: 18Years - 75Years
All Genders
NCT05886049

Testing the Addition of an Anti-cancer Drug, SNDX-5613, to the Standard Chemotherapy Treatment (Daunorubicin and Cytarabine) for Newly Diagnosed Patients With Acute Myeloid Leukemia That Has Changes in NPM1 or MLL/KMT2A Gene

Led by National Cancer Institute (NCI) · Updated on 2026-05-13

28

Participants Needed

22

Research Sites

184 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This phase Ib trial tests the safety, side effects, and best dose of SNDX-5613 when given in combination with the standard chemotherapy treatment (daunorubicin and cytarabine) in treating patients with newly diagnosed acute myeloid leukemia that has changes in the NPM1 gene or MLL/KMT2A gene. SNDX-5613 blocks signals passed from one molecule to another inside cancer cells that are needed for cancer cell survival. Drugs used in chemotherapy, such as daunorubicin and cytarabine, work in different ways to stop the growth of cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Adding SNDX-5613 to the standard chemotherapy treatment may be able to shrink or stabilize the cancer for longer than the standard chemotherapy treatment alone.

CONDITIONS

Official Title

Testing the Addition of an Anti-cancer Drug, SNDX-5613, to the Standard Chemotherapy Treatment (Daunorubicin and Cytarabine) for Newly Diagnosed Patients With Acute Myeloid Leukemia That Has Changes in NPM1 or MLL/KMT2A Gene

Who Can Participate

Age: 18Years - 75Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Patients aged 18-75 years with newly diagnosed NPM1-mutated/FLT3 wild type or MLL(KMT2A)-rearranged acute myeloid leukemia
  • Candidates for intensive induction chemotherapy
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 2 (Karnofsky score ≥ 60%)
  • Total bilirubin ≤ 2 times the upper limit of normal (ULN), except Gilbert's syndrome
  • AST/ALT ≤ 3 times ULN
  • Glomerular filtration rate (GFR) ≥ 60 mL/min/1.73 m²
  • HIV patients on effective antiretroviral therapy with undetectable viral load within 6 months
  • Patients with controlled hepatitis B or treated hepatitis C infection
  • Patients with prior or concurrent malignancies that do not interfere with safety or efficacy assessment
  • Cardiac function assessed as New York Heart Association class 2B or better
  • Ejection fraction ≥ 50% (or ≥ 45% if no heart failure symptoms) by ECHO or MUGA
  • White blood cell count less than 25 x 10⁹/L; hydroxyurea/leukapheresis allowed prior to enrollment but stopped 24 hours before treatment
  • Female patients of childbearing potential must use two forms of contraception from screening until 120 days after last treatment dose
  • Male patients with partners of childbearing potential must abstain or use two forms of contraception during the same period
  • No prior AML treatment except hydroxyurea or all-trans retinoic acid (if APL ruled out)
  • Ability to understand and sign informed consent (legally authorized representatives may consent)
Not Eligible

You will not qualify if you...

  • Allergic reactions to SNDX-5613, daunorubicin, or cytarabine
  • Uncontrolled illnesses making participation unsafe
  • Use of strong/moderate CYP3A4 inhibitors or inducers (except antifungals) or sensitive MATE1 substrates within 7 days before enrollment
  • Pregnancy or breastfeeding
  • Isolated myeloid sarcoma without blood or marrow involvement
  • Acute promyelocytic leukemia (FAB M3)
  • Active central nervous system involvement by AML
  • Uncontrolled bleeding or thrombosis due to coagulopathy
  • QTcF ≥ 450 ms or risk factors for arrhythmia unless cleared by cardiology
  • Exceeding lifetime anthracycline exposure limits
  • Upper gastrointestinal conditions affecting oral drug absorption
  • Cirrhosis with Child-Pugh score B or C
  • Down Syndrome due to increased chemotherapy toxicity risk
  • Myelodysplastic syndromes treated with intensive induction similar to 7+3 chemotherapy

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 22 locations

1

UC Irvine Health/Chao Family Comprehensive Cancer Center

Orange, California, United States, 92868

Actively Recruiting

2

University of California Davis Comprehensive Cancer Center

Sacramento, California, United States, 95817

Suspended

3

UM Sylvester Comprehensive Cancer Center at Aventura

Aventura, Florida, United States, 33180

Actively Recruiting

4

UM Sylvester Comprehensive Cancer Center at Coral Gables

Coral Gables, Florida, United States, 33146

Actively Recruiting

5

UM Sylvester Comprehensive Cancer Center at Deerfield Beach

Deerfield Beach, Florida, United States, 33442

Actively Recruiting

6

University of Miami Miller School of Medicine-Sylvester Cancer Center

Miami, Florida, United States, 33136

Actively Recruiting

7

UM Sylvester Comprehensive Cancer Center at Plantation

Plantation, Florida, United States, 33324

Actively Recruiting

8

University of Chicago Comprehensive Cancer Center

Chicago, Illinois, United States, 60637

Actively Recruiting

9

University of Kansas Clinical Research Center

Fairway, Kansas, United States, 66205

Actively Recruiting

10

University of Kansas Cancer Center

Kansas City, Kansas, United States, 66160

Actively Recruiting

11

University of Kansas Hospital-Indian Creek Campus

Overland Park, Kansas, United States, 66211

Actively Recruiting

12

University of Kansas Hospital-Westwood Cancer Center

Westwood, Kansas, United States, 66205

Actively Recruiting

13

University of Maryland/Greenebaum Cancer Center

Baltimore, Maryland, United States, 21201

Actively Recruiting

14

UNC Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, United States, 27599

Actively Recruiting

15

Carolinas Medical Center/Levine Cancer Institute

Charlotte, North Carolina, United States, 28203

Actively Recruiting

16

Wake Forest University Health Sciences

Winston-Salem, North Carolina, United States, 27157

Actively Recruiting

17

University of Cincinnati Cancer Center-UC Medical Center

Cincinnati, Ohio, United States, 45219

Actively Recruiting

18

Ohio State University Comprehensive Cancer Center

Columbus, Ohio, United States, 43210

Actively Recruiting

19

University of Cincinnati Cancer Center-West Chester

West Chester, Ohio, United States, 45069

Actively Recruiting

20

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States, 73104

Actively Recruiting

21

Huntsman Cancer Institute/University of Utah

Salt Lake City, Utah, United States, 84112

Actively Recruiting

22

University of Virginia Cancer Center

Charlottesville, Virginia, United States, 22908

Actively Recruiting

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How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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