Actively Recruiting

Phase 1
Age: 21Years - 80Years
All Genders
NCT06372821

A Trial Evaluating the Effect of NIO752 on Tau Synthesis Measured by a Process Known as SILK

Led by University College, London · Updated on 2026-01-27

10

Participants Needed

2

Research Sites

84 weeks

Total Duration

On this page

Sponsors

U

University College, London

Lead Sponsor

W

Washington University School of Medicine

Collaborating Sponsor

AI-Summary

What this Trial Is About

This study will assess if drug (NIO752) reduces production of a protein, tau, by the brain. Normally tau maintains the internal skeleton of nerve cells. In Alzheimer's disease (AD) it builds up in the brain, causing damage. Abnormal tau proteins cling to each other forming 'tangles' inside nerve cells, which interfere with how the nerve cells work, and eventually die. This is what causes the symptoms of dementia. It is thought that NIO752 reduces production of tau.

CONDITIONS

Official Title

A Trial Evaluating the Effect of NIO752 on Tau Synthesis Measured by a Process Known as SILK

Who Can Participate

Age: 21Years - 80Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Able to provide signed informed consent.
  • Between 21 to 80 years old (inclusive).
  • Diagnosed with mild or moderate Alzheimer's disease with a Clinical Dementia Rating score from 0.5 to 2, and able to complete the study.
  • History of cerebrospinal fluid, PET, or blood biomarkers supporting Alzheimer's diagnosis, or confirmed presenilin or amyloid precursor protein mutation carriers.
  • Fluent in English.
  • Has a reliable study partner or caregiver.
  • Able to undergo lumbar punctures, MRI, cerebrospinal fluid draws, and blood draws.
  • Willing to consent to sharing biological samples and personal data with the commercial partner (Novartis).
Not Eligible

You will not qualify if you...

  • Lives in a skilled nursing or dementia care facility.
  • Has any significant laboratory abnormalities.
  • Attempted suicide or had suicidal ideation requiring hospital admission within 12 months before screening.
  • Used any experimental therapy within 180 days or 5 half-lives before Day 1, whichever is longer.
  • Previously used MAPT antisense oligonucleotides or other gene therapies for Alzheimer's.
  • History of hypersensitivity to study treatments or similar drugs.
  • Has conditions increasing meningitis risk without proper prophylactic treatment.
  • Has medical or neurological conditions affecting cognition or cognitive tests.
  • Has other conditions making participation unsuitable or interfering with study completion per investigator judgment.
  • Unlikely to cooperate, attend visits, or follow instructions per investigator judgment.
  • Current alcohol intake over 14 units per week, current cannabis use, or history of substance abuse (except nicotine) within 2 years before screening.
  • Currently treated with immunosuppressants, antipsychotics, lithium, neuroleptics, dopaminergic agonists, L-dopa, or monoamine oxidase inhibitors; stable doses of cholinesterase inhibitors or memantine allowed.
  • Unable to undergo MRI due to claustrophobia or contraindications like metallic implants or pacemakers.
  • Shows significant signs of major cerebrovascular disease.
  • Sexually active males must agree to use condoms from consent until 15 weeks after treatment.
  • Breastfeeding or pregnant women, or females of reproductive potential not using highly effective contraception.
  • On regular anticoagulants or anti-platelets that prevent lumbar puncture.
  • Seropositive for HIV, Hepatitis B, or Hepatitis C.

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Trial Site Locations

Total: 2 locations

1

Washington University in St. Louis

St Louis, Missouri, United States, 63110

Actively Recruiting

2

University College London Hospitals NHS Foundation Trust

London, United Kingdom, NW1 2PG

Actively Recruiting

Loading map...

Research Team

R

Ross Paterson

CONTACT

L

Lisa French

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

TRIPLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here