Actively Recruiting

Phase 3
Age: 16Years - 70Years
All Genders
ID07363720

A Double-blind, Placebo-Controlled, Randomized Withdrawal Trial to Evaluate the Efficacy and Safety of TAK-861 for Narcolepsy With Cataplexy (Narcolepsy Type 1)

Led by Takeda · Updated on 2026-05-08

88

Participants Needed

18

Research Sites

N/A

Total Duration

On this page

AI-Summary

What this Trial Is About

Researchers are evaluating the drug TAK-861 for treating narcolepsy type 1, also known as narcolepsy with cataplexy. The study aims to understand how well TAK-861 works and whether its effects last over time. It also looks at the safety of TAK-861 and any side effects that might occur when starting or stopping the medication. All participants start by taking TAK-861 during an open-label treatment period. After this, those who meet specific criteria are randomly assigned to either continue TAK-861 at the same dose or switch to a placebo for up to 4 weeks in a double-blind randomized withdrawal period. If participants’ symptoms worsen during this time, they may stop the study treatment and have the option to join a long-term extension study or be followed for 4 weeks after stopping the drug. Participants will be involved for about 31 weeks, undergoing assessments of sleepiness using the Epworth Sleepiness Scale and other tests like the Maintenance of Wakefulness Test and Psychomotor Vigilance Test. Researchers will monitor symptom changes, cataplexy rates, and any adverse events throughout. Safety and efficacy data are collected regularly to understand how TAK-861 affects narcolepsy symptoms over time.

CONDITIONS

Brief Title

A Trial of TAK-861 for the Treatment of Narcolepsy With Cataplexy

Who Can Participate

Age: 16Years - 70Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Body mass index (BMI) between 18 and 40 kg/m²
  • Diagnosed with narcolepsy type 1 according to ICSD-3 or ICSD-3-TR criteria
  • Positive for HLA-DQB1*06:02 genotype or cerebrospinal fluid OX/hypocretin-1 concentration of 110 pg/mL or less (or less than one-third of normal values)
Not Eligible

You will not qualify if you...

  • Having another medical disorder causing excessive daytime sleepiness
  • History of myocardial infarction
  • History of significant liver, thyroid, heart rhythm, or heart failure disorders
  • Unstable cardiovascular, pulmonary, kidney, or gastrointestinal diseases
  • Current or recent (within 6 months) gastrointestinal disease affecting drug absorption
  • History of cancer within the last 5 years
  • Significant history of head injury or trauma
  • History of epilepsy, seizure, or convulsion (except single febrile seizure in childhood)
  • History of cerebral ischemia, transient ischemic attack within 5 years, intracranial aneurysm, or arteriovenous malformation

AI-Screening

AI-Powered Screening

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

Open-label Treatment Period

Duration - Approximately 16 weeks

Participants take TAK-861 to assess effectiveness and safety for narcolepsy type 1.

Double-blind Randomized Withdrawal Period

Duration - Up to 4 weeks

Participants who meet criteria are randomized to receive TAK-861 or placebo to evaluate maintenance of treatment effect.

Up to 4 weeks of treatment with visits as scheduled during withdrawal period

Follow-up

Duration - 4 weeks after last dose

Participants who discontinue treatment are followed for safety and symptom monitoring.

Follow-up visits during 4 weeks after treatment ends

Trial Site Locations

Total: 18 locations

1

Takeda Site 1

Redwood City, California, United States, 94063

Actively Recruiting

2

Takeda Site 4

Brandon, Florida, United States, 33511

Actively Recruiting

3

Takeda Site 6

Miami, Florida, United States, 33155

Actively Recruiting

4

Takeda Site 7

Southfield, Michigan, United States, 48075

Actively Recruiting

5

Takeda Site 16

Middletown, New Jersey, United States, 07748

Actively Recruiting

6

Takeda Site 17

Durham, North Carolina, United States, 27710-4000

Actively Recruiting

7

Takeda Site 18

Winston-Salem, North Carolina, United States, 27103

Actively Recruiting

8

Takeda Site 2

Cincinnati, Ohio, United States, 45245

Actively Recruiting

9

Takeda Site 15

Cleveland, Ohio, United States, 44195

Actively Recruiting

10

Takeda Site 3

Columbia, South Carolina, United States, 29201

Actively Recruiting

11

Takeda Site 5

Austin, Texas, United States, 78731

Actively Recruiting

12

Takeda Site 8

Montpellier, France, 34295

Actively Recruiting

13

Takeda Site 9

Paris, France, 75013

Actively Recruiting

14

Takeda Site 10

Toulouse, France, 31059

Actively Recruiting

15

Takeda Site 11

Schwerin, Mecklenburg-Vorpommern, Germany, 19053

Actively Recruiting

16

Takeda Site 12

Heemstede, Netherlands, 2103 SW

Actively Recruiting

17

Takeda Site 13

Barmelweid, Canton of Aargau, Switzerland, 5017

Actively Recruiting

18

Takeda Site 14

Bern, Switzerland, 3010

Actively Recruiting

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Research Team

T

Takeda Contact

How is the study designed?

Study Type

INTERVENTIONAL

Masking

DOUBLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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