Actively Recruiting

Phase 2
Age: 18Years +
All Genders
NCT04216524

Venetoclax, SL-401, and Chemotherapy for the Treatment of Blastic Plasmacytoid Dendritic Cell Neoplasm

Led by M.D. Anderson Cancer Center · Updated on 2026-04-14

40

Participants Needed

1

Research Sites

343 weeks

Total Duration

On this page

Sponsors

M

M.D. Anderson Cancer Center

Lead Sponsor

N

National Cancer Institute (NCI)

Collaborating Sponsor

AI-Summary

What this Trial Is About

This phase II trial studies how well venetoclax, SL-401, and chemotherapy works in treating patients with blastic plasmacytoid dendritic cell neoplasm. Venetoclax may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth. SL-401 is a recombinant protein consisting of IL-3 linked to a toxic agent called DT. IL-3 attaches to IL-3 receptors on tumor cells in a targeted way and delivers DT to kill them. Drugs used in chemotherapy work in different ways to stop the growth of tumor cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Giving venetoclax and SL-401 with chemotherapy may be an effective treatment for patients with blastic plasmacytoid dendritic cell neoplasm.

CONDITIONS

Official Title

Venetoclax, SL-401, and Chemotherapy for the Treatment of Blastic Plasmacytoid Dendritic Cell Neoplasm

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Patients with newly diagnosed or relapsed/refractory blastic plasmacytoid dendritic cell neoplasm confirmed by 2016 WHO criteria
  • Frontline patients may have had emergency chemotherapy or one prior cycle of SL-401 or other BPDCN therapy
  • Relapsed/refractory patients must have had at least one prior therapy cycle
  • Age 18 years or older
  • ECOG performance status of 0, 1, or 2
  • Adequate organ function including albumin 63.2 g/dL, serum creatinine <1.5 times the upper limit of normal, AST and ALT <2.5 times the upper limit of normal, and total bilirubin <1.5 times the upper limit of normal (with exceptions for Gilbert's disease or BPDCN-related elevations)
  • Ability to understand and willing to sign informed consent
  • Able to follow study visit schedule and protocol requirements including survival follow-up
  • Women of child-bearing potential and men must agree to use effective contraception during and for 2 months after treatment; males must avoid sperm donation during and for 8 weeks after last SL-401 dose
  • Left ventricular ejection fraction above institutional lower limit of normal by MUGA scan or echocardiogram within 30 days before treatment start
Not Eligible

You will not qualify if you...

  • Pregnant or breastfeeding individuals
  • Known active hepatitis B or C infection or HIV seropositivity
  • Major surgery or radiation therapy within 14 days before first study dose
  • Symptomatic or untreated leptomeningeal disease or spinal cord compression
  • Active severe heart disease (NYHA class 3 or 4), unstable angina, stroke, or heart attack within last 6 months
  • Conditions causing malabsorption or preventing oral medication intake
  • Other serious medical or psychiatric conditions or lab abnormalities that increase risk or interfere with study participation or results

AI-Screening

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Trial Site Locations

Total: 1 location

1

M D Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

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Research Team

N

Naveen Pemmaraju

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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