Actively Recruiting

Early Phase 1
Age: 18Years +
All Genders
NCT05804227

Window-of-Opportunity Trial of Ulixertinib for MAPK-Activated Gliomas

Led by M.D. Anderson Cancer Center · Updated on 2026-02-27

40

Participants Needed

1

Research Sites

230 weeks

Total Duration

On this page

Sponsors

M

M.D. Anderson Cancer Center

Lead Sponsor

B

BioMed Valley Discoveries, Inc

Collaborating Sponsor

AI-Summary

What this Trial Is About

To learn if the study drug, ulixertinib, can cross over the blood-brain barrier in patients with recurrent brain tumors

CONDITIONS

Official Title

Window-of-Opportunity Trial of Ulixertinib for MAPK-Activated Gliomas

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Willing and able to provide written informed consent (or assent with legally authorized representative if cognitively impaired)
  • Surgical cohort: 18 years or older; Non-surgical cohort: 12 years or older
  • Pediatric patients must have body surface area (BSA) of at least 0.9 m2
  • Diagnosed with MAPK-activated gliomas, mixed glioma, or glioneural tumors with certain mutations
  • Confirmed diagnosis by prior biopsy or resection; prior radiation or chemotherapy required for low-grade and oligodendroglioma patients; prior radiation required for high-grade glioma patients
  • Progressive disease per RANO criteria and presence of resectable tumor for surgical cohort
  • Progressive disease per RANO criteria for non-surgical cohort
  • At least 12 weeks from radiation therapy with evidence of disease progression
  • Any number of prior relapses allowed
  • Willing to provide archival tissue sample with required slides or tissue block
  • Performance status of 60 or higher on Karnofsky Performance Scale
  • If on steroids, stable or decreasing dose for one week prior to screening MRI; maximum 16 mg dexamethasone or equivalent daily
  • Adequate organ function as defined by laboratory values within 14 days prior to treatment
  • Negative pregnancy test for females of childbearing potential within 14 days prior to enrollment
  • Agree to use effective contraception during study and for 90 days after last treatment for males and females of childbearing potential
Not Eligible

You will not qualify if you...

  • Treatment with bevacizumab less than 3 months before enrollment
  • Presence of implanted chemotherapy (except if previously resected)
  • Less than 12 weeks since completing radiotherapy unless disease progression confirmed
  • Participation in another investigational drug or device study for therapy
  • Severe immunodeficiency or systemic immunosuppressive therapy (except steroids) within 7 days prior to study entry
  • Prior chemotherapy or targeted therapy within 3 weeks prior to study start or unresolved adverse events from previous treatment
  • Known additional progressing malignancy requiring active treatment (exceptions apply)
  • Active infection requiring systemic therapy
  • Conditions or abnormalities that could interfere with study results or participation
  • Psychiatric or substance abuse disorders interfering with study cooperation
  • Pregnant, breastfeeding, or planning to conceive or father children during the study
  • Contraindications for MRI
  • Not eligible for non-emergent surgical tumor removal
  • Taking prohibited medications that cannot be stopped before enrollment
  • History or risk of retinal vein occlusion or central serous retinopathy

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 1 location

1

M D Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

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Research Team

N

Nazanin Majd, MD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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