Clinical genetics of amyotrophic lateral sclerosis: what do we really know?
Peter M Andersen, Ammar Al-Chalabi
https://pubmed.ncbi.nlm.nih.gov/21989245Actively Recruiting
Led by Rigshospitalet, Denmark · Updated on 2017-10-06
375
Participants Needed
8
Research Sites
N/A
Total Duration
R
Rigshospitalet, Denmark
Lead Sponsor
Z
Zealand University Hospital
Collaborating Sponsor
Amyotrophic Lateral Sclerosis (ALS) is a severe, progressive disease that destroys nerve pathways controlling muscle movements, leading to difficulties in moving, breathing, swallowing, and speaking. The cause of ALS is unknown, and there is currently no treatment that stops its progression. Researchers are investigating the role of the innate immune system, especially the complement system, in the development and progression of ALS, aiming to better understand the disease and potentially guide future treatments. This project includes four clinical trials involving ALS patients, neurological controls, and healthy volunteers. Blood and spinal fluid samples are collected and stored in a biobank for analysis of complement activity and immune system components. Some ALS patients provide samples every six months to track disease progression, and a subset donates muscle biopsies to study complement activity in neuromuscular junctions. The trials use modern techniques to examine immune responses and their relation to ALS symptoms. Participants will undergo blood sampling, spinal fluid collection, and in some cases, muscle biopsies. Researchers measure complement activity, inflammatory proteins, cytokines, and muscle fiber characteristics. The study includes repeated assessments over time for some patients. Results will be analyzed statistically and published. The research aims to improve understanding of ALS pathophysiology, which may help develop targeted treatments in the future. Participation involves regular visits and sample collections over several years.
CONDITIONS
Amyotrophic Lateral Sclerosis and the Innate Immune System
You may qualify if you...
You will not qualify if you...
Complete this quick 3-step screening to check your eligibility
Duration - 2 to 4 weeks
Participants are screened for eligibility to participate in the trial.
1 visit (in-person)
Duration - Single timepoint with possible repeat sampling
Participants provide blood and spinal fluid samples which are collected and stored in a research biobank for analysis of the complement system and immune markers.
1 visit (in-person) for sample collection
Duration - Repeated every 6 months over up to 10 years
A subset of participants with ALS provide blood and spinal fluid samples every six months to monitor complement system activity as the disease progresses.
Visits every 6 months
Duration - Single timepoint with analysis over up to 3 years
A smaller subset of ALS participants undergo muscle biopsies to analyze neuromuscular junction complement activity and muscle fiber pathology.
1 visit (in-person) for biopsy
Total: 8 locations
1
Dept. of Neurology Aarhus Hospital, Nørrebrogade
Aarhus, Denmark, 8000
Actively Recruiting
2
Gildhøj Private Hospital
Brøndby, Denmark, 2605
Completed
3
Clinic of neuroanestesiology, Rigshospitalet Glostrup
Copenhagen, Denmark, 2600
Actively Recruiting
4
Dept. of Neurology, Bisbebjerg Hospital
Copenhagen NV, Denmark, 2400
Actively Recruiting
5
Clinic of Neurosurgery, Rigshospitalet
Copenhagen Ø, Denmark, 2100
Not Yet Recruiting
6
The Dept. og Neurology, Rigshospitalet Glostrup
Glostrup Municipality, Denmark, 2600
Actively Recruiting
7
Dept. of Neurology, Odense Hospital
Odense C, Denmark, 5000
Actively Recruiting
8
The dept. of Neurology, Roskilde Hospital
Roskilde, Denmark, 4000
Actively Recruiting
A
Anne-Lene Kjældgaard, MD
Study Type
OBSERVATIONAL
Masking
N/A
Allocation
N/A
Model
N/A
Primary Purpose
N/A
Number of Arms
3
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