Actively Recruiting
ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
Led by American Thrombosis and Hemostasis Network · Updated on 2026-01-12
3000
Participants Needed
71
Research Sites
791 weeks
Total Duration
On this page
Sponsors
A
American Thrombosis and Hemostasis Network
Lead Sponsor
P
Pfizer
Collaborating Sponsor
AI-Summary
What this Trial Is About
In parallel with the growth of ATHN's clinical studies, the number of new therapies for all blood disorders is increasing significantly. Some of the recently FDA-approved therapies for congenital and acquired hematologic conditions have not yet demonstrated long-term safety and effectiveness beyond the pivotal trials that led to their approval. In addition, results from well controlled, pivotal studies often cannot be replicated once a therapy has been approved for general use.2,3,4,5 In 2019 alone, the FDA has issued approvals for 24 new therapies for congenital and acquired hematologic conditions.6 In addition, almost 10,000 new studies for hematologic diseases are currently registered on www.clinicaltrials.gov.7 With this increase in potential new therapies possible, it is imperative that clinicians and clinical researchers in the field of non-neoplastic hematology have a uniform, secure, unbiased, and enduring method to collect long-term safety and efficacy data. As emphasized in a recently published review, accurate, uniform and quality national data collection is critical in clinical research, particularly for longitudinal cohort studies covering a lifetime of biologic risk.8
CONDITIONS
Official Title
ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Any age
- Having a congenital or acquired blood disorder
- Having a bleeding phenotype indicated by an age adjusted abnormal ISTH Bleeding Assessment Tool score with unknown diagnosis
- Connective tissue disorder with bleeding tendency indicated by an age adjusted abnormal ISTH Bleeding Assessment Tool score
- Eligible for a currently active disease-specific arm
- Concurrent enrollment in the ATHNdataset or current ATHNdataset participant
You will not qualify if you...
- Does not qualify for inclusion in a currently active disease-specific arm
- Unable to give informed consent or assent
- Unwilling to perform study procedures
AI-Screening
AI-Powered Screening
Complete this quick 3-step screening to check your eligibility
Trial Site Locations
Total: 71 locations
1
Arizona Hemophilia and Thrombosis Treatment Center at Phoenix Children's Hospital
Phoenix, Arizona, United States, 85016
Actively Recruiting
2
Arkansas Center for Bleeding Disorders
Little Rock, Arkansas, United States, 72202
Actively Recruiting
3
Orthopaedic Institute for Children HTC
Los Angeles, California, United States, 90007
Actively Recruiting
4
Childrens Hospital Los Angeles
Los Angeles, California, United States, 90027-6016
Actively Recruiting
5
UCSF Benioff Children's Hospital Oakland
Oakland, California, United States, 94610
Actively Recruiting
6
University of California at Davis Hemophilia Treatment Center
Sacramento, California, United States, 95817
Actively Recruiting
7
Loma Linda Hemoglobinopathy and Inherited Bleeding Disorder Program
San Bernardino, California, United States, 92408
Actively Recruiting
8
Hemophilia & Thrombosis Treatment Center at UC San Diego Health
San Diego, California, United States, 92121
Actively Recruiting
9
Rady Children's Hospital San Diego
San Diego, California, United States, 92123
Actively Recruiting
10
University of California, San Francisco Hemophilia & Thrombosis Center
San Francisco, California, United States, 94143
Actively Recruiting
11
Connecticut Children's Medical Center
Hartford, Connecticut, United States, 06106
Actively Recruiting
12
Yale Hemophilia Treatment Center
New Haven, Connecticut, United States, 06520
Actively Recruiting
13
Delaware Hemophilia Treatment Center
Wilmington, Delaware, United States, 19801
Actively Recruiting
14
Georgetown University
Washington D.C., District of Columbia, United States, 20007
Actively Recruiting
15
Children's National Hemophilia Center
Washington D.C., District of Columbia, United States, 20010
Actively Recruiting
16
University of Florida Hemophilia Treatment Center
Gainesville, Florida, United States, 32610
Actively Recruiting
17
University of Miami Comprehensive Hemophilia Treatment Center
Miami, Florida, United States, 33136
Actively Recruiting
18
Arnold Palmer Hospital for Children - The Haley Center for Children's Cancer and Blood Disorders
Orlando, Florida, United States, 32806
Not Yet Recruiting
19
Johns Hopkins All Children's Hospital
St. Petersburg, Florida, United States, 33701
Actively Recruiting
20
St. Joseph's Hospital Center for Bleeding & Clotting Disorders
Tampa, Florida, United States, 33607
Actively Recruiting
21
Comprehensive Bleeding Disorders Center at Emory University and Children's Healthcare of Atlanta
Atlanta, Georgia, United States, 30308
Actively Recruiting
22
Emory/Children's Health Care of Atlanta
Atlanta, Georgia, United States, 30322
Actively Recruiting
23
Memorial Health University Medical Center
Savannah, Georgia, United States, 31403
Actively Recruiting
24
Rush University Medical Center
Chicago, Illinois, United States, 60612
Actively Recruiting
25
Bleeding and Clotting Disorders Institute
Peoria, Illinois, United States, 61664
Actively Recruiting
26
Indiana Hemophilia and Thrombosis Center
Indianapolis, Indiana, United States, 46260
Actively Recruiting
27
Iowa Hemophilia and Thrombosis Center
Iowa City, Iowa, United States, 52242
Actively Recruiting
28
Louisiana Center for Bleeding and Clotting Disorders, Tulane University
New Orleans, Louisiana, United States, 70112
Actively Recruiting
29
Maine Hemophilia and Thrombosis Center
Scarborough, Maine, United States, 04074
Actively Recruiting
30
Johns Hopkins University Hemophilia Treatment Center
Baltimore, Maryland, United States, 21287
Actively Recruiting
31
Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center
Boston, Massachusetts, United States, 02114
Not Yet Recruiting
32
Central Michigan Children's Hospital of Michigan
Detroit, Michigan, United States, 48201
Actively Recruiting
33
Henry Ford Health System Bleeding and Thrombosis Treatment Center
Detroit, Michigan, United States, 48202
Actively Recruiting
34
Mayo Comprehensive Hemophilia Center
Rochester, Minnesota, United States, 55905
Actively Recruiting
35
Children's Mercy Hospital - Kansas City
Kansas City, Missouri, United States, 64108
Actively Recruiting
36
The John Bouhasin Center for Children with Bleeding Disorders
St Louis, Missouri, United States, 63104
Actively Recruiting
37
Cure 4 The Kids Foundation
Las Vegas, Nevada, United States, 89135
Actively Recruiting
38
Hemostasis and Thrombosis Center of Nevada
Reno, Nevada, United States, 89509
Actively Recruiting
39
Newark Beth Israel Medical Center - Hemophilia Center
Newark, New Jersey, United States, 07122
Actively Recruiting
40
University of New Mexico Ted R. Montoya Hemophilia & Thrombosis Program
Albuquerque, New Mexico, United States, 87131
Actively Recruiting
41
Western New York BloodCare
Buffalo, New York, United States, 14202
Actively Recruiting
42
Northwell Health Hemostasis and Thrombosis Center at Long Island Jewish and Cohen Children's Medical Center
Hyde Park, New York, United States, 11040
Actively Recruiting
43
Weill Cornell Medical College - New York Presbyterian Hospital
New York, New York, United States, 10065
Actively Recruiting
44
American Thrombosis and Hemostasis Network
Rochester, New York, United States, 14626
Actively Recruiting
45
Montefiore Medical Center
The Bronx, New York, United States, 10461
Actively Recruiting
46
Comprehensive Hemophilia Treatment Center, University of North Carolina at Chapel Hill
Chapel Hill, North Carolina, United States, 27517
Actively Recruiting
47
St. Jude Affiliate Clinic at Novant Health Hemby Children's Hospital
Charlotte, North Carolina, United States, 28204
Actively Recruiting
48
East Carolina University Hemophilia Treatment Center
Greenville, North Carolina, United States, 27834
Actively Recruiting
49
Wake Forest University Health Sciences
Winston-Salem, North Carolina, United States, 27157
Actively Recruiting
50
Akron Children's Hospital - Showers Center for Cancer & Blood Disorders
Akron, Ohio, United States, 44308
Actively Recruiting
51
Cincinnati Children's Hospital Medical Center, Hemophilia & Thrombosis Center
Cincinnati, Ohio, United States, 45229
Actively Recruiting
52
University of Cincinnati Medical Center Hemophilia Treatment Center
Cincinnati, Ohio, United States, 45267
Actively Recruiting
53
University Hospitals Health System Cleveland
Cleveland, Ohio, United States, 44106
Actively Recruiting
54
Nationwide Children's Hospital Columbus
Columbus, Ohio, United States, 43205
Actively Recruiting
55
Dayton Children's Hemostasis and Thrombosis Center
Dayton, Ohio, United States, 45404
Actively Recruiting
56
Northwest Ohio Hemophilia Treatment Center at the Toledo Hospital
Toledo, Ohio, United States, 43606
Actively Recruiting
57
Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, United States, 19104
Actively Recruiting
58
Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania
Philadelphia, Pennsylvania, United States, 19104
Actively Recruiting
59
Hemophilia Center of Western Pennsylvania
Pittsburgh, Pennsylvania, United States, 15213
Actively Recruiting
60
Rhode Island Hospital Hemostasis and Thrombosis Center
Providence, Rhode Island, United States, 02903
Actively Recruiting
61
St. Jude Children's Research Hospital
Memphis, Tennessee, United States, 38105
Actively Recruiting
62
Vanderbilt University Medical Center
Nashville, Tennessee, United States, 37212
Actively Recruiting
63
Children's Blood and Cancer Center of Central Texas
Austin, Texas, United States, 78723
Actively Recruiting
64
North Texas Hemophilia and Thrombosis Program - Pediatric Program / Center for Cancer & Blood Disorders
Dallas, Texas, United States, 75235
Actively Recruiting
65
North Texas Comprehensive Hemophilia Treatment Center
Dallas, Texas, United States, 75390
Actively Recruiting
66
Gulf States Hemophilia and Thrombophilia Center
Houston, Texas, United States, 77030
Actively Recruiting
67
Texas Children's Hemophilia & Thrombosis Center/Baylor College of Medicine
Houston, Texas, United States, 77030
Actively Recruiting
68
South Texas Comprehensive Hemophilia and Thrombophilia Treatment Center
San Antonio, Texas, United States, 78229
Actively Recruiting
69
Washington Center for Bleeding Disorders
Seattle, Washington, United States, 98101
Actively Recruiting
70
Hemophilia Outreach Center Green Bay
Green Bay, Wisconsin, United States, 54311
Actively Recruiting
71
Comprehensive Center for Bleeding Disorders
Milwaukee, Wisconsin, United States, 53226
Actively Recruiting
Research Team
C
Carol Fedor, ND, RN, CCRC
CONTACT
N
Nana Ama Afari-Dwamena, MPH
CONTACT
How is the study designed?
Study Type
OBSERVATIONAL
Masking
N/A
Allocation
N/A
Model
N/A
Primary Purpose
N/A
Number of Arms
7
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