Actively Recruiting

Age: 0 - 15Years
All Genders
NCT06212947

A Multicenter Multinational Observational Study of Children With Hypochondroplasia

Led by BioMarin Pharmaceutical · Updated on 2025-04-03

400

Participants Needed

43

Research Sites

1048 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This study will assess growth over time and the clinical course of HCH in children by collecting growth measurements and other variables of interest.

CONDITIONS

Official Title

A Multicenter Multinational Observational Study of Children With Hypochondroplasia

Who Can Participate

Age: 0 - 15Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Participants must be 64 15 years old at the time of signing the informed consent
  • Participants must have genetic confirmation of Hypochondroplasia diagnosis
Not Eligible

You will not qualify if you...

  • Have a diagnosis of another genetic short stature condition other than Hypochondroplasia or a genetic variant known to cause another genetic syndrome associated with short stature
  • Received an investigational product or medical device within 6 months before the Screening visit

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 43 locations

1

Phoenix Children's Hospital

Phoenix, Arizona, United States, 85016

Actively Recruiting

2

Cedars-Sinai Medical Center

Los Angeles, California, United States, 90048

Not Yet Recruiting

3

UCSF Benioff Children's Hospital

Oakland, California, United States, 94609

Actively Recruiting

4

Nemours Alfred I. Dupont Hospital for Children

Wilmington, Delaware, United States, 19803

Actively Recruiting

5

Children's National Health System

Washington D.C., District of Columbia, United States, 20010

Actively Recruiting

6

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States, 60611

Actively Recruiting

7

The Johns Hopkins University School of Medicine

Baltimore, Maryland, United States, 21218

Not Yet Recruiting

8

Boston Children's Hospital

Boston, Massachusetts, United States, 02115

Actively Recruiting

9

University of Minnesota Masonic Children's Hospital

Minneapolis, Minnesota, United States, 55454

Actively Recruiting

10

University of Missouri

Columbia, Missouri, United States, 65212

Actively Recruiting

11

Washington University School of Medicine in St. Louis

St Louis, Missouri, United States, 63110

Actively Recruiting

12

Mount Sinai Kravis Children's Hospital

New York, New York, United States, 10029

Actively Recruiting

13

Akron Children's Hospital

Akron, Ohio, United States, 44307

Not Yet Recruiting

14

Nationwide Children's Hospital

Columbus, Ohio, United States, 43205

Not Yet Recruiting

15

Cook Children's Endocrinology

Fort Worth, Texas, United States, 76104

Actively Recruiting

16

Medical College of Wisconsin, Children's Hospital

Milwaukee, Wisconsin, United States, 53226

Actively Recruiting

17

Hospital de Pediatria SAMIC Prof. Dr. Juan P Garrahan

Buenos Aires, Argentina

Not Yet Recruiting

18

Royal Children's Hospital Melbourne

Parkville, Victoria, Australia, 3052

Actively Recruiting

19

Hospital de Clinicas de Porto Algre

Porto Alegre, Rio Grande Do Sol, Brazil

Not Yet Recruiting

20

Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto

Ribeirão Preto, São Paulo, Brazil

Not Yet Recruiting

21

Stollery Children's Hospital

Edmonton, Alberta, Canada

Actively Recruiting

22

SickKids - The Hospital for Sick Children

Toronto, Ontario, Canada

Actively Recruiting

23

Centre Hospitalier Universitaire Sainte-Justine

Montreal, Quebec, Canada

Not Yet Recruiting

24

Hospices Civils de Lyon - Hôpital Femme Mère Enfant

Lyon, France

Actively Recruiting

25

Hopital de la Timone

Marseille, France

Actively Recruiting

26

Hôpital Necker-Enfants Malades

Paris, France

Actively Recruiting

27

CHU de Toulouse - Hopital des Efants

Toulouse, France

Actively Recruiting

28

Uniklinik Koln

Cologne, Germany

Actively Recruiting

29

Universitatskinderklinik Magdeburg

Magdeburg, Germany

Actively Recruiting

30

Istituto Giannina Gaslini

Genoa, Liguria, Italy

Actively Recruiting

31

Ospedale Pediatrico Bambino Gesù

Roma, Rome, Italy

Not Yet Recruiting

32

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, Italy

Actively Recruiting

33

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Rome, Italy

Actively Recruiting

34

Kumamoto University Hospital

Kumamoto, Kumamoto, Japan

Actively Recruiting

35

Osaka University Hospital

Suita, Osaka, Japan

Actively Recruiting

36

Tottori University Hospital

Yonago, Tottori, Japan

Actively Recruiting

37

Tokushima University Hospital

Tokushima, Japan

Not Yet Recruiting

38

Institute of Science Tokyo Hospital

Tokyo, Japan

Actively Recruiting

39

Hospital Universitario La Paz

Madrid, Spain

Actively Recruiting

40

Vithas Hospital San Jose

Vitoria-Gasteiz, Spain

Actively Recruiting

41

Great Ormond Street Hospital for Children NHS Foundation Trust

London, England, United Kingdom

Actively Recruiting

42

Myriad Trials Ltd

London, England, United Kingdom

Not Yet Recruiting

43

NHS Greater Glasgow and Clyde

Glasgow, Scottland, United Kingdom

Actively Recruiting

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Research Team

T

Trial Specialist

CONTACT

How is the study designed?

Study Type

OBSERVATIONAL

Masking

N/A

Allocation

N/A

Model

N/A

Primary Purpose

N/A

Number of Arms

1

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A Multicenter Multinational Observational Study of Children With Hypochondroplasia | DecenTrialz