Actively Recruiting
Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
Led by AstraZeneca · Updated on 2026-05-05
1850
Participants Needed
60
Research Sites
391 weeks
Total Duration
On this page
Sponsors
A
AstraZeneca
Lead Sponsor
I
ICON plc
Collaborating Sponsor
AI-Summary
What this Trial Is About
The MaesTTRo study aims to enroll a global cohort of patients with transthyretin (ATTR) amyloidosis to longitudinally observe the natural course of the disease and describe real-world treatment patterns and outcomes. In addition, information on the effectiveness of ATTR amyloidosis treatments, including eplontersen, which is a ligand-conjugated antisense oligonucleotide gene silencing treatment targeting activity against both the mutant and wild-type TTR protein, will be collected.
CONDITIONS
Official Title
Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Patient willing and able to provide written informed consent to participate in the study
- Confirmed diagnosis of amyloid transthyretin (ATTR) amyloidosis
- Aged 18 years or older at the time of signing the informed consent
- Patient willing and able to participate in collection of electronic patient reported outcomes (PROs)
You will not qualify if you...
- Concurrent participation in any interventional trial for ATTR amyloidosis
- Involvement in the planning and/or conduct of the current study
- Patients with evidence of primary or light chain amyloidosis (AL) or serum protein A amyloidosis (AA)
- Asymptomatic patients with ATTR amyloidosis and asymptomatic ATTR mutation carriers
AI-Screening
AI-Powered Screening
Complete this quick 3-step screening to check your eligibility
Trial Site Locations
Total: 60 locations
1
Research Site
La Jolla, California, United States, 92037
Actively Recruiting
2
Research Site
Los Angeles, California, United States, 90095
Actively Recruiting
3
Research Site
San Francisco, California, United States, 94025
Actively Recruiting
4
Research Site
San Francisco, California, United States, 94143
Actively Recruiting
5
Research Site
New Haven, Connecticut, United States, 06510
Actively Recruiting
6
Research Site
Washington D.C., District of Columbia, United States, 20010
Actively Recruiting
7
Research Site
Chicago, Illinois, United States, 60637
Actively Recruiting
8
Research Site
Indianapolis, Indiana, United States, 06200
Actively Recruiting
9
Research Site
Boston, Massachusetts, United States, 02111
Actively Recruiting
10
Research Site
Boston, Massachusetts, United States, 02114
Not Yet Recruiting
11
Research Site
Boston, Massachusetts, United States, 02115
Actively Recruiting
12
Research Site
Rochester, Minnesota, United States, 55905
Actively Recruiting
13
Research Site
Kansas City, Missouri, United States, 64111
Actively Recruiting
14
Research Site
St Louis, Missouri, United States, 63110
Actively Recruiting
15
Research Site
New Brunswick, New Jersey, United States, 08901
Actively Recruiting
16
Research Site
Manhasset, New York, United States, 11030
Actively Recruiting
17
Research Site
New York, New York, United States, 10027
Actively Recruiting
18
Research Site
New York, New York, United States, 10029
Actively Recruiting
19
Research Site
Durham, North Carolina, United States, 27710
Actively Recruiting
20
Research Site
Danville, Pennsylvania, United States, 17822
Actively Recruiting
21
Research Site
Philadelphia, Pennsylvania, United States, 19104
Actively Recruiting
22
Research Site
Philadelphia, Pennsylvania, United States, 19107
Actively Recruiting
23
Research Site
Greenville, South Carolina, United States, 29607
Actively Recruiting
24
Research Site
Germantown, Tennessee, United States, 38138
Actively Recruiting
25
Research Site
Nashville, Tennessee, United States, 037214
Actively Recruiting
26
Research Site
Dallas, Texas, United States, 75246
Actively Recruiting
27
Research Site
Richmond, Virginia, United States, 23298
Actively Recruiting
28
Research Site
Seattle, Washington, United States, 98915
Actively Recruiting
29
Research Site
Milwaukee, Wisconsin, United States, 53226
Actively Recruiting
30
Research Site
Vancouver, British Columbia, Canada, V5Z 1M9
Actively Recruiting
31
Research Site
Vancouver, British Columbia, Canada, V6Z 1Y6
Actively Recruiting
32
Research Site
Halifax, Nova Scotia, Canada, B3RIV9
Actively Recruiting
33
Research Site
London, Ontario, Canada, N6A 5A5
Actively Recruiting
34
Research Site
Toronto, Ontario, Canada, M2J 4W8
Actively Recruiting
35
Research Site
Rimouski, Quebec, Canada, G5L 5T1
Not Yet Recruiting
36
Research Site
Beijing, Beijing Municipality, China, 100034
Not Yet Recruiting
37
Research Site
Beijing, Beijing Municipality, China, 100191
Not Yet Recruiting
38
Research Site
Beijing, Beijing Municipality, China, 100730
Actively Recruiting
39
Research Site
Changsha, Hunan, China, 410013
Not Yet Recruiting
40
Research Site
Shanghai, Shanghai Municipality, China, 200040
Actively Recruiting
41
Research Site
Hebei Sheng, Shijiazhuang, China, 050000
Not Yet Recruiting
42
Research Site
Shaanxi, Xi'An, China, 710061
Actively Recruiting
43
Research Site
Würzburg, Bavaria, Germany, DE-97072
Not Yet Recruiting
44
Research Site
Frankfurt am Main, Hesse, Germany, 60590
Actively Recruiting
45
Research Site
Hanover, Lower Saxony, Germany, 30625
Actively Recruiting
46
Research Site
Aachen, North Rhine-Westphalia, Germany, 52074
Actively Recruiting
47
Research Site
Cologne, North Rhine-Westphalia, Germany, 50937
Actively Recruiting
48
Research Site
Mainz, Rhineland-Palatinate, Germany, 55131
Actively Recruiting
49
Research Site
Homburg, Saarland, Germany, 66421
Actively Recruiting
50
Research Site
Berlin, Germany, 10117
Actively Recruiting
51
Research Site
Huelva, Andalusia, Spain, 21005
Actively Recruiting
52
Research Site
Cataluna, Barcelona, Spain, 08907
Not Yet Recruiting
53
Research Site
Bilbao, Basque Country, Spain, 48013
Actively Recruiting
54
Research Site
Las Palmas de Gran Canaria, Canary Islands, Spain, 35010
Actively Recruiting
55
Research Site
Salamanca, Castille and León, Spain, 37007
Actively Recruiting
56
Research Site
Barcelona, Catalu A, Spain, 08035
Actively Recruiting
57
Research Site
Islas Baleares, Palma de Mallorca, Spain, 07198
Actively Recruiting
58
Research Site
Birmingham, West Midlands, United Kingdom, B15 2GW
Actively Recruiting
59
Research Site
Glasgow, United Kingdom, G51 4TF
Actively Recruiting
60
Research Site
London, United Kingdom, NW3 2QG
Actively Recruiting
Research Team
A
AstraZeneca Clinical Study Information Center
CONTACT
How is the study designed?
Study Type
OBSERVATIONAL
Masking
N/A
Allocation
N/A
Model
N/A
Primary Purpose
N/A
Number of Arms
3
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